The FDA found that data from a single Phase II study were “insufficient” to justify an accelerated approval review for sevasemten in Becker muscular dystrophy.

The death of a boy with Duchenne muscular dystrophy, tied to a gene therapy, is above all a tragedy. But it is also undermining investor confidence in the company that makes it.

Pentacam and corneal topography were more sensitive to tear film abnormalities when measuring the curvature of the cornea in those with dry eye.

The research aimed to identify how neurodevelopmental and psychiatric conditions associated with dystrophinopathy, including DMD and Becker muscular dystrophy (BMD), were assessed.

Corneal ulcers are most common in contact lens wearers, but they also occur as complications of many conditions. Learn what they are and how to lower your risk.

Design Therapeutics Announces Favorable Phase 1 Data for DT-168 Supporting Advancement into Phase 2 Biomarker Trial for Patients with Fuchs Endothelial Corneal Dystrophy ...

Design Therapeutics will present DT-168 program updates for Fuchs endothelial corneal dystrophy at Eyecelerator on May 2, 2025.

In addition to its GeneTAC ® programs, DT-216P2, in development for patients with Friedreich ataxia, and DT-168, for Fuchs endothelial corneal dystrophy, the company is advancing programs in ...

An expanded clinical trial that tested an experimental stem cell treatment for blinding cornea injuries found the treatment was feasible and safe in 14 patients who were treated and followed for ...

A new therapy repairs corneal damage to a patient's eye using stem cells from their other, healthy eye.

Fuchs’ Corneal Dystrophy Causes and Risk Factors The innermost layer of your cornea, called the endothelium, removes fluids from the cornea to keep it clear.

Corneal dystrophies are a group of rare diseases that cause build-up of foreign matter in the layers of the cornea. Some lead to vision loss. Learn more.