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6 Therapies on the Horizon for Spinal Muscular Atrophy
Since 2016, the FDA has approved three disease-modifying treatments for spinal muscular atrophy, with several ...
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Novartis Reports Updated Positive Data From Phase III SMA Program
The early to mid-stage dose-ranging study evaluated the safety and efficacy of the candidate in patients with SMA with three ...
Scientists Solve One of Genomics’ Biggest Challenges by Using HiFi Sequencing to Distinguish Highly Similar Paralogous Genes
Detailed price information for Pacific Biosciences (PACB-Q) from The Globe and Mail including charting and trades.
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Scientists Solve One of Genomics’ Biggest Challenges by Using HiFi Sequencing to Distinguish Highly Similar Paralogous Genes
These regions contain hundreds of genes critical to human health—including those implicated in spinal muscular atrophy (SMN1/SMN2), congenital adrenal hyperplasia (CYP21A2), and red-green color ...