Myrtelle’s candidate is rAAV-Olig001-ASPA, a gene therapy for Canavan disease (CD), a ... white matter of the brain to degenerate. People with VWM disease commonly have symptoms such as impaired ...

U.S. aid cuts could jeopardize the supply of donated drugs that are hailed for their effectiveness in combating neglected ...

Epidermolysis bullosa is a rare and severe skin disease where patients have fragile skin that blisters and tears. A Mt.

Early access via large-scale clinical study to establish the validity and utility of the FirstGene TM screen ...

Use precise geolocation data and actively scan device characteristics for identification. This is done to store and access ...

Many rare disease patients do not receive a formal genetic diagnosis, but a European data-sharing project aimed to give them ...

The funeral will take place on Thursday of Maureen Walsh, the mother of Westlife manager and former X factor judge and ...

Delivered by a dedicated team of healthcare professionals trained in exercise assessment, prescription and progression, with experience of delivering patient-focused education on chronic respiratory ...