Interim results from a small group of children in a Phase I/II trial are essentially in line with that of Elevidys, according ...

In many genetic diseases, a small error in the DNA code can have devastating effects. These errors, called nonsense mutations ...

Despite recent declines, we believe Pfizer stock is a compelling buy right now, with its current price of around $23 likely ...

Dystrophin's isoforms are thought to contribute variably to neuropsychiatric disorders, behavioral disorders, and ...

Cardiac complications in Duchenne muscular dystrophy (DMD) are the result of cardiac muscle involvement that accompanies the ...

The American Journal of Managed Care provides insights into the latest news and research in managed care across multimedia ...

Advancements in gene therapy for Duchenne muscular dystrophy (DMD) have improved the outlook for some patients, but further ...

But, the longevity of the treatment is a concern for providers ... of treating patients earlier.” Though there is no requirement for DMD newborn screening in Arizona, Castle has been active ...

Satellos CEO Frank Gleeson said: “Given the short 28-day treatment window ... of functional muscle tissue. There are some approved gene therapies for DMD, including Roche and Sarepta’s ...

With additional steps being taken at the federal level to limit fluoride intake, what could that mean for Americans?

This cardiomyopathy eventually leads to heart failure, which is currently the leading cause of death among those with DMD. Treatment options are limited and there is no cure. Deramiocel (CAP-1002 ...

which is currently the leading cause of death among those with DMD. Treatment options are limited and there is no cure. Deramiocel (CAP-1002) consists of allogeneic cardiosphere-derived cells (CDCs), ...