The custom-built gene editing treatment for 6-month-old KJ Muldoon could not have come at a more welcome or jarring time for CRISPR-powered biomedicine.

NEWS 19 May 2025 Correction 19 May 2025 World first: ultra-powerful CRISPR treatment trialled in a person Immune-cell function improved in a teenager whose DNA was altered using prime editing.

A CRISPR treatment seems to have been effective for a baby’s devastating disease, but it is not clear whether such bespoke therapies can be widely applied ...

Scientists were able to create a bespoke treatment for KJ Muldoon’s rare genetic disorder within six months. It could be a blueprint for potentially life-saving, gene-editing Crispr therapies.

In a world first, scientists used CRISPR to fix a baby's unique genetic mutation. The report offers hope for personalized treatments of rare diseases.

Doctors hope baby KJ will avoid the need for a liver transplant after CRISPR therapy.

World’s first personalized CRISPR therapy given to baby with genetic disease Treatment seems to have been effective, but it is not clear whether such bespoke therapies can be widely applied.

Discover how hemophilia A affects blood clotting, its genetic patterns, warning signs, advanced treatment options, and lifestyle modifications ...

In a medical first, doctors raced to create a bespoke CRISPR gene therapy for a boy born with a deadly genetic disease and delivered it to him a mere six and a half months after birth. The CRISPR ...

Haemophilia Treatment: Union science and technology minister Jitendra Singh reviewed progress in the work during an inspection of facilities at BRIC-inStem. "This is a milestone in India's ...

The FDA has approved Qfitlia (fitusiran) for routine prophylaxis to prevent or reduce the frequency of bleeding episodes in patients with hemophilia A or hemophilia B.