With gene therapy offering new hope for thalassemia, experts urge Indian govt to invest in early diagnosis, genetic testing, ...

Thalassemia, a group of inherited blood disorders characterized by reduced or abnormal hemoglobin production, continues to ...

A four-year-old Pakistani girl diagnosed with severe thalassemia has been successfully treated with a Chinese-developed ...

In medical breakthrough, a baby diagnosed with rare genetic disorder is thriving after customized CRISPR gene editing therapy ...

Geneticists have used a cutting-edge DNA base editing treatment on several patients to cure thalassemia, a prevalent and severe genetic blood disease.

G ene therapy has always held enormous promise to correct genetic diseases, but turning that potential into treatments has been challenging.

Editas Medicine reports successful gene editing levels in stem cells, supporting potential treatment for sickle cell disease and beta thalassemia. Editas Medicine announced promising new data on ...

Anemia raises your risk of organ damage and death. Beta thalassemia is treatable. You can manage it with blood transfusions, a treatment called iron chelation therapy, and by staying healthy.

The FDA approved betibeglogene autotemcel (beti-cel; Zynteglo) for adult and pediatric patients with transfusion-dependent beta-thalassemia in August 2022, and exagamglogene autotemcel (exa-cel ...

and exagamglogene autotemcel (Casgevy)-- have been approved for treating beta-thalassemia. While this is "very exciting," Brodsky pointed out that treatment with gene therapy still requires a ...

Called Casgevy, the gene-editing treatment is for people with sickle cell disease and a related blood disorder called beta thalassemia. UK regulators approved the treatment in November 2023 ...