Gene therapy has always held enormous promise to correct genetic diseases, but turning that potential into treatments has ...

Anemia raises your risk of organ damage and death. Beta thalassemia is treatable. You can manage it with blood transfusions, a treatment called iron chelation therapy, and by staying healthy.

Researchers have found a promising new method for gene therapy. They successfully restarted inactive genes by bringing them ...

This article describes how beta thalassemia is passed from parent to child, the symptoms that can occur, and when treatment is needed. Carrying or Inheriting the Beta Thalassemia Minor Trait The ...

and exagamglogene autotemcel (Casgevy)-- have been approved for treating beta-thalassemia. While this is "very exciting," Brodsky pointed out that treatment with gene therapy still requires a ...

The treatment, the doctors said, is potentially curative, though they noted that it's too new to definitively call it a cure for beta thalassemia. A similar process will be used to treat people ...

A 19-year-old severe thalassemia patient has recently become China's first successful case cured through cell and gene therapy at Nansha Hospital of Guangzhou First Municipal People's Hospital. This ...

Nabeel was born with an inherited blood disorder called beta thalassemia ... like a really big blessing," Rahemeen Nabeel said. The treatment includes chemotherapy that allows the gene therapy ...

KJ Muldoon, a 10-month-old baby, was diagnosed with the genetic disease carbamoyl-phosphate synthetase 1 deficiency after he ...

New gene therapy improves the life of 18-year-old with Sickle Cell Disease which affects 5,000 New Jersey residents living with the condition.