Limited micro-mapping has shown an uneven distribution in frequencies of beta thalassemia carriers in different districts in Maharashtra (1-6%) and Gujarat (0-9.5%) within small geographic regions.

The FDA has accepted the sNDA for mitapivat for the treatment of non-transfusion-dependent and transfusion-dependent alpha- or beta-thalassemia.

FDA Accepts Agios’ Supplemental New Drug Application for PYRUKYND® (mitapivat) in Adult Patients with Non-Transfusion-Dependent and Transfusion-Dependent Alpha- or Beta-Thalassemia ...

Such forward-looking statements include those regarding the potential benefits of PYRUKYND® (mitapivat); Agios’ expectations for the FDA’s review of its sNDA for PYRUKYND® in alpha-and-beta ...

The interaction of this "silent" form of beta thalassemia with high hemoglobin A 2 thalassemia results in thalassemia major of reduced severity.

Thalassemia is a genetic blood disorder that impacts the ability of the blood to get oxygen to the body’s organs. Learn about the signs, how it’s diagnosed & treated.

These materials are the first internationally available CRMs developed to help identify carriers and patients with beta-thalassemia and are an important step forward in the fight against the disease.

Here’s hoping that our list of 55 Gen Alpha slang words will give you some cool points with the youth. It will also give you some clue as to what these kids are saying.

Agios is hoping for a broad label in thalassemia, covering both alpha and beta subtypes regardless of transfusion dependence. They estimate that this market (18+) is 6,000 in the US.

CONVINCING evidence has been presented that the term thalassemia does not describe a specific or homogeneous entity. Bather, it refers to a group of heritable defects of hemoglobin synthesis manife ...

Thalassemia carriers typically do not experience thalassemia symptoms, but they may experience anemia symptoms, such as fatigue and skin paleness. Learn more here.