This study identifies astrocyte-intrinsic mechanisms by which the LRRK2 G2019S, a mutation linked to familial Parkinson's disease, disrupts synaptic integrity in the anterior cingulate cortex. The ...

Eli Lilly will acquire gene-editing startup Verve Therapeutics for up to $1.3 billion, the companies said on Tuesday, accelerating a push into experimental cardiovascular therapies.

Penn researchers believe new potential gene therapy for glioblastoma brain cancer offers ‘a lot of hope’ Glioblastoma has been deadly and hard to treat, but researchers say they’ve made progress with ...

Gene therapy experts and advocates warning of the sector’s many challenges found a receptive audience in FDA leadership at a regulatory forum Thursday.

Baby KJ Muldoon, the first patient to successfully receive personalized CRISPR gene editing therapy has returned home after over 300 days at the hospital.

A team of doctors at the Children's Hospital of Philadelphia and Penn Medicine treated a baby with a gene editing technology customized for his rare disease for the first time ever.

Baby saved by gene-editing therapy 'graduates' from hospital, goes home KJ Muldoon was diagnosed with a rare, deadly genetic disease after he was born.

After spending over 300 days at CHOP, KJ Muldoon has been released from the hospital after receiving personalized CRISPR gene editing therapy.

A Better Understanding of How Gene Editing Tools Work New research shows that certain cell proteins can help or hurt base editing ...

Abstract Horizontal gene transfer by natural transformation (NT) is induced in Vibrio cholerae upon attachment to chitin surfaces in the aquatic environment. Here, we show that free environmental DNA ...

Clinical Trials Demonstrate Monitoring PD-L1 Upregulation Using LifeTracDx Blood Test Could Support New Treatment Path for Metastatic Triple Negative Breast Cancer ...

RMAT designation expected to expedite development; 72 weeks interim clinical trial data showing sustainable reduction of TTR over 90% with no significant adverse events. SUZHOU, China, May 29, 2025 ...