It will grow to $9.02 billion in 2029 at a compound annual growth rate (CAGR) of 15.3%.” — The Business Research Company LONDON, GREATER LONDON, UNITED KINGDOM, July 3, 2025 /EINPresswire.com/ -- Save ...

Novartis is on the final straight to approval of its spinal muscular atrophy (SMA) gene therapy Zolgensma in the EU, after getting a recommendation for approval from the CHMP. The positive opinion ...

Both drugs are designed to switch on the SMN2 gene, to compensate for the loss of the SMN1 gene that isn't working properly in SMA, but Novartis found that its drug also worked on another gene ...

Panelists discuss how spinal muscular atrophy is an autosomal recessive genetic disease affecting motor neurons with 3 ...

Paraphase – a computational tool that accurately resolves and analyzes paralogous genes – unlocks the difficult-to-analyze ...

Gene Demby is a founding member of NPRs Code Switch team, where he serves as a host of the show's podcast. In 2020, Code Switch was named Apple's inaugural Podcast Of The Year. Demby's essays for ...

In perhaps a first in the country, a newborn found carrying the SMN1 gene mutation for Spinal Muscular Atrophy (SMA) through prenatal genetic screening is being administered presymptomatic ...

Eli Lilly & Co. agreed to buy Verve Therapeutics Inc., a US biotech that’s seeking to use gene editing to prevent clogged arteries, for as much as $1.3 billion.

Gene expression is the generation of a functional gene product from the information encoded by a gene, through the processes of transcription and translation. Gene products are often proteins ...

Alsheebani's care team at The James, led by Dr. Marcos de Lima and Dr. Roberta Azbell, employed gene therapy to treat Alsheebani's illness by injecting him with a medication that allows stem cells ...

Parents of kids with rare gene disorder raise £70k Collect/PA Real Life Parents Mel and Charlie organise events through their charity, Cure DHDDS, to raise money for treatment 12 June 2025 ...

Klotho Neurosciences, Inc. (NASDAQ: KLTO), a U.S.-based biogenetics company announced the findings of pre-clinical studies indicating the potential of elevating Klotho gene expression to ...