Maintaining good metabolic control, especially in adolescence, can help to optimize cognitive development in adults with PKU. A rare metabolic disease, PKU is caused by a deficiency in ...

These therapies don’t work for all PKU patients and some who take Palynziq struggle to maintain the required regimen of daily injections. For 2023, BioMarin reported $484.7 million in combined ...

Ajinomoto Cambrooke, Inc., a global leader in medical nutrition, proudly celebrates its 25th anniversary with an expanded ...

Eton promotes PKU GOLIKE with its existing metabolic sales force, which also promotes Eton’s Carglumic Acid, Betaine, and Nitisinone products.

Relief Therapeutics Holding SA / Key word(s): Study results Relief Therapeutics Announces Final Readout of PKU GOLIKE Clinic ...

The BriefA Pinellas County mother of a 4-year-old boy diagnosed with a rare metabolic disorder is pushing for more accessible ...

Inborn errors of metabolism (IEMs) are rare, devastating disorders caused by pathogenic variants in genes encoding key metabolic enzymes, ... Differentiate the efficacy of base-editing solutions for ...

RELIEF THERAPEUTICS Holding SA, a biopharmaceutical company committed to delivering innovative treatment options for select specialty, unmet and rare diseases, announced today that interim data ...

JINAN, China, June 23, 2025 /PRNewswire/ -- On May 29, 2025, Professor Sun Jinpeng's team and Professor Yu Xiao's team at Shandong University, collaborating with Professor Jiang Changtao from ...