The approval is based on Phase 3 EPIDYS trial data that demonstrated meaningful treatment benefits in ambulant patients ...

DMD commonly affects boys, where symptoms are seen in early childhood. There is no cure for DMD. Health care providers manage symptoms with steroids, physical therapy, and assistive devices (like ...

They can also have heart and lung problems. Although there isn't a cure, the outlook for people with DMD is better than it has ever been. Years ago, children with the disease usually didn’t live ...

Interim results from a small group of children in a Phase I/II trial are essentially in line with that of Elevidys, according ...

Not only that, but there is no guarantee that the company will be able to receive U.S. marketing approval of deramiocel for the treatment of patients with DMD cardiomyopathy. The second risk to ...

The American Journal of Managed Care provides insights into the latest news and research in managed care across multimedia ...

Repurposing existing therapies may help slow muscle weakness in patients with Duchenne muscular dystrophy, a new study ...

You may need to see a specialist if your child is having difficulty swallowing. There is no known cure for DMD. Treatment aims to control symptoms to improve quality of life. Several new ...

Cardiac complications in Duchenne muscular dystrophy (DMD) are the result of cardiac muscle involvement that accompanies the ...

The added genetic code will then start producing dystrophin, the protein lacking in patients with muscular dystrophy. Currently, there is no cure for the disease and available treatments and drugs ...