Crypto billionaire Brian Armstrong is ready to invest in CRISPR baby tech Brian Armstrong ... specialists to form a founding team for an “embryo editing” effort targeting an unmet medical ...

Researchers from the Centenary Institute have uncovered a reason why some people with hemophilia A develop resistance to their critical treatment, paving the way for the development of more ...

Marstacimab is the first under the skin (subcutaneous) injection for severe haemophilia B and today’s decision comes just weeks after the treatment received its UK licence. Given as a once-weekly ...

The only gene-editing therapy currently on the market is a CRISPR–Cas9-based treatment for two blood disorders, sickle-cell disease and β-thalassaemia. This costs more than US$2 million per ...

Getting treatment to KJ quickly was critical for doctors. Researchers at the University of California, Berkeley and the Children’s Hospital of Philadelphia worked together to test a CRISPR base ...

Just six months later, he received a Crispr treatment designed just for him. Muldoon has a rare disorder known as CPS1 deficiency, which causes a dangerous amount of ammonia to build up in the blood.

Instead, at 6 months, doctors administered the first dose of the gene editing treatment. They have since been able to loosen a strict low-protein diet and reduce his daily ammonia-lowering ...

Haemophilia is a genetic blood disorder in which blood doesn't clot normally, causing abnormal bleeding. Union science and technology minister Jitendra Singh reviewed progress in the work during ...

March 31, 2025 – The FDA has approved a new drug as a preventive treatment to reduce bleeding episodes in people with certain types of hemophilia. This first-of-its-kind injectable drug offers ...

The ATLAS-INH trial included male patients with severe hemophilia A or B with inhibitors who were receiving on-demand treatment with bypassing agents (BPA). Study participants were randomly ...

Beam Therapeutics said Monday that it used a form of CRISPR called base editing to ... Three patients who received a high dose of Beam’s treatment saw their levels of AAT rise to an average ...