In the first part of this series, we explored how early genetic screening and gene therapy transform the lives of newborns ...

As newborn screening and rapid DNA sequencing become routine, we are poised to catch and treat inherited diseases at their ...

Machine learning models have seeped into the fabric of our lives, from curating playlists to explaining hard concepts in a ...

A 5-year-old boy from Center City has faced rare odds since birth and now this warrior is in a real life race to rewrite his story.

The personalized CRISPR treatment could be the future of gene therapy, but hurdles remain before everyone has access.

Scientists at the San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), Milan, have found that gene editing using ...

In comments posted in response to the Trump administration’s pharma tariff investigation, companies and industry groups ...

Advancements in gene therapy for Duchenne muscular dystrophy (DMD) have improved the outlook for some patients, but further ...

Qure divested for $25M, advanced AMT-130 with FDA approvals, and building infrastructure. A strong balance sheet backs ...

In this video, Jay Chhablani, MD, discusses preliminary data from the ArMaDa study of OCU410 gene therapy for geographic atrophy presented at the ARVO meeting.

This study reveals the potential of engineered phage-IL-12 therapy in melanoma, enhancing immune response and tumor ...

Needham raised its price target for Taysha Gene Therapies Inc. (NASDAQ:TSHA) to $8 from $6, while maintaining a Buy rating on ...