MicroRNA-33a and microRNA-33b are encoded within the mammalian SREBF1 and SRBF2 genes, respectively, and both SREBF1 and ...

Background Glucocorticosteroids (GC) are standard-of-care treatment for most boys with duchenne muscular dystrophy (DMD). GC use has changed over time with evolving evidence, and we describe GC ...

In many biological systems, the sample's morphological information cannot be perfectly captured simultaneously by a single image acquisition due to the limited dynamic range of the detector. Here, we ...

The company said it was optimistic that the issues identified by the Food and Drug Administration could be resolved with new data.

Introduction: Duchenne/Becker muscular dystrophies (DMD/BMD) are inherited muscle diseases, collectively referred to as dystrophinopathy, which are characterized by progressive degeneration or loss.

Physical activity and rehabilitation are key components of Duchenne muscular dystrophy treatment, despite recent drug therapy advances. "Rehabilitation care and rehabilitation teams with ...

The existing methods can only display grayscale images or scrolling display binary images, and they cannot scroll the display of grayscale image which required to be completed in scanning maskless ...

Precision may also be eligible to receive a Priority Review Voucher upon FDA approval of PBGENE-DMD.

Published data support the drug's effectiveness in motor and respiratory outcomes (13, 66). The advantage of newborn screening and presymptomatic diagnosis was proven in the SPRINT trial including ...