Dystrophin's isoforms are thought to contribute variably to neuropsychiatric disorders, behavioral disorders, and ...

RegenXBio has shared updated phase 1/2 data on its Duchenne muscular dystrophy (DMD) gene therapy, providing evidence that ...

Edgewise Therapeutics faces challenges with DMD/BMD programs, upcoming trial data concerns, and competitive risks.

Advancements in gene therapy for Duchenne muscular dystrophy (DMD) have improved the outlook for some patients, but further ...

The American Journal of Managed Care provides insights into the latest news and research in managed care across multimedia ...

Repurposing existing therapies may help slow muscle weakness in patients with Duchenne muscular dystrophy, a new study ...

"Nomination and acceleration of PBGENE-DMD as our second wholly owned program is a result of the compelling preclinical evidence we have generated to date," said Michael Amoroso, President and ...

Entrada Therapeutics has secured the Health Authorities and Ethics Committees' authorisation within the European Union (EU) ...

People with a DMD diagnosis must believe this isn’t a sign to roll the end credits on their lives, says Luca Buccella. Even before he learned of his Duchenne Muscular Dystrophy (DMD) diagnosis ...

Diagnosed with Duchenne muscular dystrophy (DMD) at three years old, Dr Jon Hastie grew up never thinking about the future – until one day he discovered he actually had one. Now in his 30s ...