A new paper published in Gene Therapy raises serious concerns about the effectiveness of gene therapy for Duchenne muscular ...

Barry Byrne, MD, PhD, Powell Gene Therapy Center at the University of Florida, discusses gene therapy considerations for pediatric patients and how newborn screening can influence outcomes for ...

Sarepta Therapeutics announced that a patient with Duchenne muscular dystrophy who received Elevidys (delandistrogene moxeparvovec-rokl) died following treatment.

Italfarmaco’s oral HDAC inhibitor givinostat has been approved in the US as a treatment for Duchenne muscular dystrophy (DMD), becoming the first non-steroidal option for patients with all ...

Sarepta is currently testing SRP-9001 in the placebo-controlled EMBARK study, which aims to enrol 120 boys with DMD aged four to seven and is due to read out in the latter half of 2023.

This approach can help prevent interference with ongoing conversations or landing you in the dentist’s chair for a root canal. Another issue I’ve come across is seeing the same Task reoccur ...

Good oral hygiene is an important part of staying healthy so having a capable dentist you trust is vital. If you’re unhappy with your dental care or think you've been misled in regards to the cost of ...

Our comparison table, based on prices from major private chains, gives you an idea of what to expect. NHS dentist prices typically go up slightly each year. These are the prices from April 2025 for ...

KER-065, a potential treatment for Duchenne muscular dystrophy (DMD) and other neuromuscular diseases, showed a good safety profile in a Phase 1 clinical trial. No serious side effects were seen in ...