Discover the current pipeline candidates advancing through the clinic for the treatment of sickle cell disease.

A team of astronomers has uncovered an unexpectedly complex and dynamic filamentary network within a very-high-velocity cloud ...

This study reports the important development and characterization of next-generation analogs of the molecule AA263, which was previously identified for its ability to promote adaptive ER proteostasis ...

New University of Virginia School of Medicine research suggests an unexpected way doctors may be able to improve blood flow to the brain to battle Alzheimer's and other neurodegenerative diseases.

Fragile X disorders include two distinct conditions: fragile X syndrome (the most common single-gene cause of developmental delay and autism) and an entirely separate group of premutation syndromes.