Leaders from the world of cell and gene therapy shared their personal stories and policy recommendations in an extraordinary roundtable conducted by the FDA in front of its recently-appointed top ...

Victoria Gray is the first person in the world to receive CRISPR,  a gene-editing therapy for sickle cell disease created by ...

A team of scientists from the San Raffaele-Telethon Institute for Gene Therapy (SR-Tiget) in Milan, Italy, has identified a ...

Researchers have identified an early postnatal window that allows gene transfer to circulating blood stem cells, advancing ...

Unlike existing treatments for Alzheimer’s that target unhealthy protein deposits, the new approach developed at UC San Diego ...

Machine learning models have seeped into the fabric of our lives, from curating playlists to explaining hard concepts in a ...

A team of scientists from the San Raffaele-Telethon Institute for Gene Therapy (SR-Tiget) in Milan, Italy, has identified a ...

The sale of bluebird bio and Pfizer’s decision to drop a gene therapy for hemophilia have led to some anxiety regarding the future of cell and gene therapy (CGT). As the chief executive officer ...

CGT Catapult is an independent technology and innovation organization specializing in the advancement of the cell and gene therapy industry. It was established by and works in partnership with ...

But in December, Beauzile, 21, became the first person in New York State to be made symptom-free of sickle cell disease after undergoing Lyfgenia, a new type of gene therapy that uses stem cell ...

A Fayetteville teen is making history in North Carolina after undergoing a new gene therapy for sickle cell disease. Aaron Scott was diagnosed with sickle cell at birth. Sickle cell is a genetic ...