Ultragenyx Pharmaceuticals RARE announced that the FDA has granted the Breakthrough Therapy designation to its ...

Taysha Gene Therapies, Inc. (NASDAQ:TSHA) is one of the 10 best healthcare penny stocks to buy according to analysts.

In a conversation with People magazine in 2024, Colin Farrell opened up for the first time about his son's rare condition: ...

Angelman syndrome is a rare condition that causes problems with growth and development. It’s caused by a genetic mutation (a change in your genes) that affects the nervous system. It’s named ...

A Georgia woman declared brain dead gave birth to a premature baby via emergency cesarean section. The baby, named Chance, is in the NICU and expected to recover.

ATLANTA — The baby of a woman in Georgia who was declared brain dead and has been on life support since February was delivered early Friday morning, her mother said. April Newkirk told WXIA-TV that 31 ...

This cover image depicts a human brain with colorful microplastic particles scattered across its surface, juxtaposed with a white plastic spoon as a visual representation. Research has revealed that ...

The girl's symptoms have worsened since the family of mixed-immigration status was deported to Mexico in February, her mother told NBC News exclusively. “We’re fighting for my girl’s life." ...

CARLSBAD, CA, USA I June 11, 2025 I Ionis Pharmaceuticals, Inc. (Nasdaq: IONS) today announced that the first participant has been dosed in the global Phase 3 REVEAL study, which is designed to ...

Ionis Pharmaceuticals has dosed the first subject in the global, randomised Phase III REVEAL trial of investigational ION582, aimed at treating individuals with Angelman syndrome (AS), a rare ...

More information: Benjamin J Buehner et al, Medial temporal lobe atrophy in Down syndrome along the Alzheimer's disease continuum, Brain (2025). DOI: 10.1093/brain/awaf133 ...

For his part, Mr Trump said during the spat that Mr Musk suffered from “Trump Derangement Syndrome”, brought on by how much he missed working for the president.