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Thalassemia is a genetic blood disorder that impacts the ability of the blood to get oxygen to the body’s organs. Learn about the signs, how it’s diagnosed & treated.
Feeling tired and weak all the time and having pale or yellowish skin may be connected to your genes. Alpha thalassemia is an inherited blood disorder in which specific gene mutations that get ...
In beta thalassemia, the beta globin genes are affected. Each of these forms of thalassemia has different subtypes. The exact form you have will affect the severity of your symptoms and your outlook.
The sNDA is supported by data from the phase 3 ENERGIZE and ENERGIZE-T studies, which evaluated mitapivat vs placebo in patients with NTD and TD alpha- or beta-thalassemia, respectively.
The JRC has now released a new CRM to aid the fight against beta-thalassemia. This genetic blood disorder reduces the production of haemoglobin, the iron-containing protein in red blood cells ...
Mitapivat was associated with a significant reduction in transfusion burden in adults with transfusion-dependent (TD) alpha- or beta-thalassemia, according to results from the phase 3 ENERGIZE-T ...
Alpha-thalassemia is one of the most common hemoglobin genetic abnormalities and is caused by the reduced or absent production of the alpha globin chains. Alpha-thalassemia is prevalent in ...
People with alpha thalassemia can experience chest pain, drowsiness, and dizziness. In beta thalassemia, there is delayed growth (in kids), skeletal deformities, excessive iron, increased ...
The US Food and Drug Administration has approved a second use for the first CRISPR-based medicine, Casgevy, which was approved in December to treat sickle cell disease. CNN values your feedback 1.