Gomekli is the first medication approved for both adult and pediatric patients with NF1-PN. The Food and Drug Administration (FDA) has approved Gomekli â„¢ (mirdametinib) for the treatment of ...
Feb. 12, 2025 – The FDA has approved a new pill for a rare genetic disorder called neurofibromatosis type 1 (NF1). It is for adults and children ages 2 and older who have nerve tumors ...
It’s important to know that an accurate diagnosis of NF1 can only be made by a physician with expertise in the diagnosis and treatment of neurofibromatosis. Because people with NF1 often have multiple ...