Anemia raises your risk of organ damage and death. Beta thalassemia is treatable. You can manage it with blood transfusions, a treatment called iron chelation therapy, and by staying healthy.

KJ Muldoon, a 10-month-old baby, was diagnosed with the genetic disease carbamoyl-phosphate synthetase 1 deficiency after he ...

Gene therapy has always held enormous promise to correct genetic diseases, but turning that potential into treatments has ...

Geneticists have used a cutting-edge DNA base editing treatment on several patients to cure thalassemia, a prevalent and ...

This article describes how beta thalassemia is passed from parent to child, the symptoms that can occur, and when treatment is needed. Carrying or Inheriting the Beta Thalassemia Minor Trait The ...

New gene therapy improves the life of 18-year-old with Sickle Cell Disease which affects 5,000 New Jersey residents living ...

A four-year-old Pakistani girl diagnosed with severe thalassemia has been successfully treated with a Chinese-developed ...

With gene therapy offering new hope for thalassemia, experts urge Indian govt to invest in early diagnosis, genetic testing, ...

Nabeel was born with an inherited blood disorder called beta thalassemia ... like a really big blessing," Rahemeen Nabeel said. The treatment includes chemotherapy that allows the gene therapy ...